Rocket Pharmaceuticals (@rocketpharma) 's Twitter Profile
Rocket Pharmaceuticals

@rocketpharma

Seeking #GeneTherapy cures for patients with rare and devastating diseases.

ID: 1192460341533454336

linkhttps://www.rocketpharma.com/ calendar_today07-11-2019 15:15:19

632 Tweet

985 Followers

208 Following

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TOMORROW – Join our #RareDiseaseDay event livestream! Hear powerful stories from those living with a #raredisease, plus advocacy talks, educational sessions & more. See the agenda & register: eventcreate.com/e/rocket-pharm…

TOMORROW – Join our #RareDiseaseDay event livestream! Hear powerful stories from those living with a #raredisease, plus advocacy talks, educational sessions & more.

See the agenda & register: eventcreate.com/e/rocket-pharm…
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Today is the day! Don’t miss our livestreamed panel on #DanonDisease, a spotlight on RTW Charitable Foundation's impact, patient advocacy talks, and expert discussions on genetic testing and future therapies. Register: eventcreate.com/e/rocket-pharm… #RareDiseaseDay

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In honor of #RareDiseaseDay, #TeamRocket CEO Gaurav Shah and President, Head R&D and COO Kinnari Patel met at the NYSE 🏛 to discuss our pursuit of #GeneTherapy cures. Watch below and join us in working toward a future where DNA is no longer destiny. youtu.be/QnIzduHB1Fg?si…

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Our #RareDiseaseDay event was filled with powerful stories and impactful discussions. Thank you to all participants who drive progress in the #RareDisease community. To keep the momentum, #LightUpForRare today at 7 p.m.! Hang lights & decorate with theme colors to show support.

Our #RareDiseaseDay event was filled with powerful stories and impactful discussions. Thank you to all participants who drive progress in the #RareDisease community.

To keep the momentum, #LightUpForRare today at 7 p.m.! Hang lights & decorate with theme colors to show support.
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We’re thrilled to have rung the opening bell at Nasdaq on #RareDiseaseDay! We’re overwhelmed with gratitude at the opportunity to commemorate this important day & show our dedication, commitment, & mission to seek gene therapy cures for patients with devastating rare diseases.

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Seeing major buildings lit up in support of #LightUpForRare for #RareDiseaseDay was incredibly inspiring. Thank you to all who participated— together, we’re spreading awareness and sparking change. Let’s continue lighting the way for #RareDisease advocacy and progress!

Seeing major buildings lit up in support of #LightUpForRare for #RareDiseaseDay was incredibly inspiring. Thank you to all who participated— together, we’re spreading awareness and sparking change. Let’s continue lighting the way for #RareDisease advocacy and progress!
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We’re onsite at the Rare Diseases Clinical Research Network Primary Immune Deficiency Treatment Consortium. As bronze level sponsors, we’re joining others working to improve outcomes for patients with rare, life-threatening, inherited disorders of the immune system.

We’re onsite at the <a href="/rarediseasesnet/">Rare Diseases Clinical Research Network</a> Primary Immune Deficiency Treatment Consortium. As bronze level sponsors, we’re joining others working to improve outcomes for patients with rare, life-threatening, inherited disorders of the immune system.
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From our live event, to ringing the Nasdaq bell, to lighting up Empire State Building, and much more, this #RareDiseaseDay was one to remember. Thank you for supporting our mission! Watch the replay: youtube.com/watch?v=FNjmfv… Danon Disease Foundation @RareDiseaseDay RTW Charitable Foundation Make-A-Wish New Jersey

From our live event, to ringing the <a href="/Nasdaq/">Nasdaq</a> bell, to lighting up <a href="/EmpireStateBldg/">Empire State Building</a>, and much more, this #RareDiseaseDay was one to remember. Thank you for supporting our mission!

Watch the replay: youtube.com/watch?v=FNjmfv…

<a href="/DanonFoundation/">Danon Disease Foundation</a> @RareDiseaseDay <a href="/CharitableRTW/">RTW Charitable Foundation</a> <a href="/wishnj/">Make-A-Wish New Jersey</a>
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We’re heading to #ACC25 this week! We’re looking forward to joining the latest industry research, drug development, and patient discussions as we progress three AAV #GeneTherapy programs that could impact +100k patients in the U.S. and EU. More: bit.ly/3R5o8RL

We’re heading to #ACC25 this week! We’re looking forward to joining the latest industry research, drug development, and patient discussions as we progress three AAV #GeneTherapy programs that could impact +100k patients in the U.S. and EU.

More: bit.ly/3R5o8RL
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#TeamRocket is sharing poster presentations at two upcoming medical meetings: #AMCP2025 and #ISHLT2025. We look forward to connecting with fellow attendees and sharing our mission to fulfill the promise of #GeneTherapy for patients with devastating #RareDiseases. @AMCPorg The ISHLT

#TeamRocket is sharing poster presentations at two upcoming medical meetings: #AMCP2025 and #ISHLT2025. We look forward to connecting with fellow attendees and sharing our mission to fulfill the promise of #GeneTherapy for patients with devastating #RareDiseases.

@AMCPorg <a href="/ISHLT/">The ISHLT</a>
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Next week, #TeamRocket President, Head of R&D, and COO Kinnari Patel, PharmD, MBA will join a panel at the Alliance for Regenerative Medicine (ARM) Cell & Gene Meeting on the Med. Learn more: meetingonthemed.com/agenda/

Next week, #TeamRocket President, Head of R&amp;D, and COO Kinnari Patel, PharmD, MBA will join a panel at the <a href="/alliancerm/">Alliance for Regenerative Medicine (ARM)</a> Cell &amp; Gene Meeting on the Med. 

Learn more: meetingonthemed.com/agenda/
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On April 22, #TeamRocket will host a webinar with Genetic Counselors on the potential of #GeneTherapy to provide a one-time treatment for inherited cardiomyopathies, including #Danon disease, featuring Jonathan Schwartz, Chief Medical & Gene Therapy Officer. ow.ly/sNuF50Vot8b

On April 22, #TeamRocket will host a webinar with
<a href="/GeneticCouns/">Genetic Counselors</a> on the potential of #GeneTherapy to provide a one-time treatment for inherited cardiomyopathies, including #Danon disease, featuring Jonathan Schwartz, Chief Medical &amp; Gene Therapy Officer.

ow.ly/sNuF50Vot8b
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At #WorldOrphanUSA, #TeamRocket President, Head of R&D, and COO Kinnari Patel, PharmD, MBA, joins the keynote panel on the future of #RareDisease R&D to bring innovative therapies to people with rare diseases. More: terrapinn.com/conference/wor…

At #WorldOrphanUSA, #TeamRocket President, Head of R&amp;D, and COO Kinnari Patel, PharmD, MBA, joins the keynote panel on the future of #RareDisease R&amp;D to bring innovative therapies to people with rare diseases.
More: terrapinn.com/conference/wor…
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#WorldPIWeek 2025 is here! #TeamRocket is committed to raising awareness about Primary Immunodeficiencies (PI) and supporting the global PI community. We're advancing #GeneTherapy to offer hope for those impacted by #RareDiseases like LAD-I. Learn more: rocketpharma.com/patients-and-c…

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This #NationalDNADay we celebrate the impact of genomics on modern medicine. #TeamRocket is on a mission to seek gene therapy cures for patients with devastating #RareDiseases through the most innovative science and platforms. rocketpharma.com/our-science/ #DNADay #Genetics #Genomics

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This #FanconiAnemia Awareness Month, #FCF2025, #TeamRocket stands with patients and caregivers impacted by Fanconi anemia and remains committed to understanding their experience and advancing investigational new medicines. See below for more and in full: youtube.com/watch?v=3EYtwl…

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#TeamRocket is looking forward to the ASGCT annual meeting next week! We will present preliminary Phase 1 data for plakophilin-2 related arrhythmogenic cardiomyopathy (PKP2-ACM) in a late-breaking oral presentation. Learn more: bit.ly/4kbVCu7. #ASGCT2025

#TeamRocket is looking forward to the <a href="/ASGCTherapy/">ASGCT</a> annual meeting next week! We will present preliminary Phase 1 data for plakophilin-2 related arrhythmogenic cardiomyopathy (PKP2-ACM) in a late-breaking oral presentation. Learn more: bit.ly/4kbVCu7. #ASGCT2025
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#News from #ASGCT2025: #TeamRocket presents preliminary data for the first time from the Phase 1 study of RP-A601, an investigational #GeneTherapy for the treatment of plakophilin-2 related arrhythmogenic cardiomyopathy (PKP2-ACM). Learn more: bit.ly/4dmJTXx.

#News from #ASGCT2025: #TeamRocket presents preliminary data for the first time from the Phase 1 study of RP-A601, an investigational #GeneTherapy for the treatment of plakophilin-2 related arrhythmogenic cardiomyopathy (PKP2-ACM).

Learn more: bit.ly/4dmJTXx.
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Thanks to all who joined our webinar with Genetic Counselors on the power of #GeneticTesting and counseling for those impacted by inherited, #RareDiseases like #DanonDisease. Watch the replay: youtube.com/watch?v=k3R6nc….

Thanks to all who joined our webinar with <a href="/GeneticCouns/">Genetic Counselors</a> on the power of #GeneticTesting and counseling for those impacted by inherited, #RareDiseases like #DanonDisease. 

Watch the replay: youtube.com/watch?v=k3R6nc….