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Our latest paper in our mission to better treat #Duchenne postulates targeting global cytoprotectant, Nrf2. Thanks to my super team Stephanie Kourakis Cara Timpani Institute for Health and Sport, VU AIMSS & collabs Prof Judy de Haan @ukbbkinderspit1 University of Tasmania #MyoTwitter doi.org/10.1016/j.redo…

Proud of our international effort pioneering Nrf2-targeted therapeutics against #duchenne...here we compare old vs new wave corticosteroids and ponder if we have a better solution? Institute for Health and Sport, VU AIMSS @ukbbkinderspit1 University of Tasmania pubmed.ncbi.nlm.nih.gov/33663533/

Really happy to share our translational work currently under review…5 years in the making and 3 children later including twins👇 Institute for Health and Sport, VU AIMSS Victoria University Cara Timpani Stephanie Kourakis #WomeninScience biorxiv.org/content/10.110…

I couldn’t be prouder of my postdoc Cara Timpani on being awarded a Jack Brockhoff ECR Medical Research Grant to work on the gut-muscle axis. The first of many more to follow! Victoria University Institute for Health and Sport, VU AIMSS #WomenInSTEM

Excited to share perspectives on our new medicine development program for ultra-rare #adss1myopathy in collaboration with Cure ADSSL1, Dystrophy Concepts, Harvard Medical School Boston Children's Cure Rare Disease Institute for Health and Sport, VU mdpi.com/2321416 #mdpipharmaceuticals MDPI

Happy to be part of this perspective paper on adenylosuccinic acid and its potential as a therapy for ADSSL1 Myopathy. @CureADSSL1 @DystrophyConcepts Harvard Medical School Boston Children's Cure Rare Disease Institute for Health and Sport, VU mdpi.com/2321416 #mdpipharmaceuticals via MDPI

Super proud of my team's recent JCI insight paper demonstrating the potential of dimethyl fumarate for #DuchenneMuscularDystrophy with collabs esp. twitterless Dirk Fischer & Narges Dargahi Institute for Health and Sport, VU Victoria University Departement Klinische Forschung, Universität Basel insight.jci.org/articles/view/…

Hot off the press...critical toxicology work for our U.S. FDA IND application toward a clinical trial testing ASA for #RareDisease #myotwitter Adenylosuccinic Acid Is a Non-Toxic Small Molecule In Vitro and In Vivo mdpi.com/2518800 #mdpipharmaceuticals via MDPI

So very excited for our research on re-purposed dimethyl fumarate as a treatment for #Duchenne muscular dystrophy to be in JCI insight. Thanks to our wonderful collaborators and to Muscular Dystrophy Association and AFM-Téléthon for funding our research program to further explore this therapy

Excited to see our work featured in Rare Disease Advisor. Congrats Stephanie Kourakis Cara Timpani Dean Campelj PhD & collabs on an insightful paper with huge reach! Research Explores Duchenne Muscular Dystrophy Care of the Past and Present rarediseaseadvisor.com/insights/dmd-i…

Congrats Stephanie Kourakis Cara Timpani Dean Campelj PhD and team...another feature in a recent Expert Point of View by Prof Laurent Servais from Department of Paediatrics on neurodiem bit.ly/_Kourakis-et-a…

Full text here: rdcu.be/dpzHd Institute for Health and Sport, VU Victoria University AIMSS AIMSS Inherited & Acquired Myopathy Program

Excited to release our new work linking clock regulated splicing factor Rbm20 to metabolic disruption in estrogen deprived mdx muscle: Loss of endogenous estrogen alters mitochondrial metabolism and muscle clock-related protein Rbm20 in female mdx mice biorxiv.org/content/10.110…

Delighted to share new work from my lab led by Stephanie Kourakis Cara Timpani showing some nice anti-fibrotic and -adiposis effects of dimethyl fumarate in disease aggravated mdx striated muscle. #duchenne Funded by Muscular Dystrophy Association Australian Physiological Society Victoria University biorxiv.org/content/10.110…

Super excited to share our work that demonstrates the moderate-term effects of dimethyl fumarate in aggravated mdx skeletal muscle and heart! Emma Rybalka Cara Timpani #Duchenne Victoria University AIMSS Inherited & Acquired Myopathy Program biorxiv.org/content/10.110…

Super proud to receive NHMRC Ideas funding for our #rareNMD #ADSS1myopathy research. Congrats team: Cara Timpani Priyanka Kakkar and twitterless Alan Beggs, Behzad Moghadaszadeh, David Mack, Alec Smith, Benjamin Parker Wendy Hanna-Rose Victoria University vu.edu.au/about-vu/news-…

Timely insights ahead of #RareDiseaseDay! Emma Rybalka Cara Timpani ojrd.biomedcentral.com/articles/10.11…

Proud to have another chapter of my PhD out in the world! Huge thanks to my supervisors Emma Rybalka & Cara Timpani for their endless support! 💫 Repurposed Nrf2 activator dimethyl fumarate rescues muscle inflammatio... sciencedirect.com/science/articl…

Another great paper out from our lab! Congrats Dean Campelj PhD Guinevere Spiesberger Cara Timpani Emma Rybalka 🎉 Haptoglobin and Glutamine Synthetase May Biomark Cachexia Induced by Antiacute Myeloid Leukaemia Chemotherapy onlinelibrary.wiley.com/doi/10.1002/jc…