
X4 Pharmaceuticals
@x4pharma
With rare resolve, we drive progress for people living with rare immune disorders.
ID: 1181925409392340993
https://www.x4pharma.com/ 09-10-2019 13:33:31
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Did You Know? In WHIM syndrome, there is a reported median 5-year delay between the onset of symptoms and diagnosis, and for these patients, a 27% incidence of end-organ damage. Find us American Society of Pediatric Hematology/Oncology Booth 307 to learn about earlier diagnosis in pediatric patients.



That’s a wrap for X4 at the 2025 American Society of Pediatric Hematology/Oncology Conference! We’ve enjoyed our discussions with HCPs about their approaches to diagnosing and managing WHIM syndrome. Our mission to drive early diagnosis continues—find resources at bit.ly/4kiobGE. #ASPHO2025


At the upcoming European Hematology Association Congress between June 12–15, we’ll present data from our Phase 2 trial in chronic #neutropenia — our first time sharing these results with the #hematology community. Learn more about our participation: bit.ly/3S4PND2 #EHA2025


Did You Know? The Immune Deficiency Foundation reports that most patients with WHIM syndrome are first diagnosed with CVID. X4 is excited to announce the launch of WHIMsyndrome.com, where patients with questions about their immune deficiency may find answers: bit.ly/4htAkXh.


We're proud to receive the 2025 Industry Innovation Award presented by National Organization for Rare Disorders (NORD) (NORD)! At X4, we're driving progress for people living with rare immune disorders through our medicines and by advocating for the needs of patients. rareimpact.org #RareDiseases


We presented positive data from our completed Phase 2 trial of mavorixafor for the treatment of chronic #neutropenia (CN) at the European Hematology Association Congress. Review the data in today’s press release: bit.ly/4mUAtH8 #EHA2025


ICYMI – our CFO, Adam Mostafa, was recently interviewed by Informa Connect – learn more about his unique journey from Wall Street to biotech: bit.ly/4nB32tq


Proud to launch our WHIM Syndrome Patient Education Program at this year’s Neutropenia Network Conference highlighting the importance of genetic testing and early diagnosis to support improved health outcomes. #WHIMsyndrome whimsyndrome.com


Our CEO Dr. Paula Ragan recently engaged in a fireside chat with Jeanne Siegel, head of the Neutropenia Network, focused on X4’s efforts to expand treatment options for those with chronic neutropenic conditions. #neutropenia #RareResolve
