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Thank you to the staff and Board of Fabry International Network for hosting us at your excellent Expert Meeting in Lisbon! It was great to see #GeneTherapy on the agenda. And special to be there during #FabryAwrenessMonth

For #HDAwarenessMonth, EU HD advocate Sophia visited us in Basel to share her #huntingtonsdisease journey. She chooses to get the most out of life while becoming involved in the community and staying hopeful that transformative treatment options are on the way. #LetsTalkAboutHD

uniQure is proud to support the ALS community at the ALS Roundtable in Washington, DC during ALS Awareness Month. We're excited to engage with leaders and advocates to advance research and solutions for ALS. Together, we can make a difference! 💙 #ALS #ALSAwarenessMonth

A beautiful spring day celebrating #HDawarenessmonth with HDSA New England at today's Celebration of Hope brunch! As always, we are inspired by the indefatigable spirit of the #Huntingtonsdisease community and proud to lend our support to the wonderful work they do.

Today we reported our financial results for the first quarter of 2025 and highlighted recent progress across our business, including initial safety data from the third cohort of the Phase I/II study of AMT-130 in #huntingtonsdisease. uniqure.gcs-web.com/news-releases/…

On this International #HDAwareness Day, we at uniQure are grateful for the HD advocates who have shared their powerful stories with our team over the years. Their experiences inspire us in our work to deliver a transformative treatment for the #HuntingtonsDisease community.

We’ve had some bon temps in New Orleans this week at #ASGCT2025, where our team presented four posters and one oral presentation highlighting our leadership in #genetherapy research and capsid development.

This #ALSAwarenessMonth, we reflect on the words of Ron Faretra, an #ALS advocate who spoke to our employees this year. His courage and determination reflect the strength of the ALS community and inspire us in our work to deliver a transformative #genetherapy for SOD1-ALS.

Today we'll present a clinical case study of the first participant dosed in the ongoing trial of #genetherapy AMT-260 in MTLE, showing no serious adverse events and 92% reduction in seizure frequency through the first five months of follow up. #epilepsy uniqure.gcs-web.com/news-releases/…

We were happy to be a part of today's EpilepsyFoundationNE Boston Walk for #Epilepsy at historic Fenway Park. The Northeast's largest epilepsy event gave us and the NE epilepsy community a chance to walk through the beautiful neighborhood and spend time at the home of our beloved #RedSox!

Following recent Type B meetings, alignment with the FDA continues to support an Accelerated Approval pathway for AMT-130 in #Huntingtonsdisease. We've reached alignment with the FDA in several key areas, with a BLA submission expected in early 2026. uniqure.gcs-web.com/news-releases/…

uniQure is proud to support the @End_the_Legacy conference! Join us to learn about the latest in genetic ALS and our commitment to treating it. #EndTheLegacy #GeneTherapy #uniQure

CEO Matthew Kapusta talks about uniQure's mission to transform the lives of patients through the power of genetics, and how that mission drives who we are at uniQure. #genetherapy youtu.be/ltBrutxeOLg

We're thrilled to be heading to Indy as a Gold Sponsor of this year's #HDSAConvention, where we'll have a fantastic cross-functional team on hand to attend the sessions, support the #huntingtonsdisease community, and share information about our AMT-130 #genetherapy program.

Our #HDSAConvention booth is open! Come drop by this weekend to say hello, grab some snacks, and learn more about our AMT-130 #genetherapy program in #huntingtonsdisease.

The powerful candle-lighting ceremony at tonight’s HDSA National Awards Dinner & Gala was the emotional pinnacle of an inspiring evening, lighting the room with love and hope in memory of those lost and in honor of all those fighting against #huntingtonsdisease. #HDSAConvention

We were privileged to attend this past weekend’s #HDSAConvention to connect with and learn from the #huntingtonsdisease community. We return home inspired by their courage & resiliency and excited to continue our efforts to bring a transformative #genetherapy to families in need.